Lachie's Wish 4 CS
Our mission is to provide support to Christianson Syndrome patients and to drive therapeutic-discovery research forward. We are investigating gene therapy and small molecule options for Christianson Syndrome patients. Help us support this therapy and others to the clinic!

Lachie's Wish 4 CS is a 501(c)3 tax-exempt organization, and your donation is tax deductible within the guidelines of U.S. law. Please keep your receipt as your official record. We'll email it to you upon successful completion of your donation.
Check out our progress!
Want to learn more? Keep up to date on all our research progress at www.lachieswish4cs.org!
Research:
- Using an Slc9a6 shaker rat model, we hope to determine the phenotypic rescue possibilities of genetic medicine and timing of administration.
- MRI biomarker assay development for robust clinical trial endpoints.
- Motor and non-motor rescue observations to elucidate the therapeutic effect of this candidate therapy.